A protein tertiary structure mimetic modulator of the Hippo signalling pathway

November 9, 2021

Title

A protein tertiary structure mimetic modulator of the Hippo signalling pathway

Author

Helene Adihou, Ranganath Gopalakrishnan, Tim Forster, Stephanie M. Gueret, Raphael Gasper, Stefan Geschwindner, Carmen Carrillo Garcia, Hacer Karatas, Ajaybabu V. Pobbati, Mercedes Vazquez-Chantada, Paul Davey, Carola M. Wassvik, Jeremy Kah Sheng Pang, Boon Seng Soh, Wanjin Hong, Elisabetta Chiarparin, Dennis Schade, Alleyn T. Plowright, Eric Valeur, Malin Lemurell, Tom N. Grossmann & Herbert Waldman

Year

2021

Journal

Nature Communications

Abstract

Transcription factors are key protein effectors in the regulation of gene transcription, and in many cases their activity is regulated via a complex network of protein–protein interactions (PPI). The chemical modulation of transcription factor activity is a long-standing goal in drug discovery but hampered by the difficulties associated with the targeting of PPIs, in particular when extended and flat protein interfaces are involved. Peptidomimetics have been applied to inhibit PPIs, however with variable success, as for certain interfaces the mimicry of a single secondary structure element is insufficient to obtain high binding affinities. Here, we describe the design and characterization of a stabilized protein tertiary structure that acts as an inhibitor of the interaction between the transcription factor TEAD and its co-repressor VGL4, both playing a central role in the Hippo signalling pathway. Modification of the inhibitor with a cell-penetrating entity yielded a cell-permeable proteomimetic that activates cell proliferation via regulation of the Hippo pathway, highlighting the potential of protein tertiary structure mimetics as an emerging class of PPI modulators.

Instrument

V-550, J-715

Keywords

protein, tertiary structure, PPI, interactions,